Hematopoietic stem cell transplantation in 746 children with osteopetrosis: A study of the inborn errors working party of the EBMT

Robert Chiesa(Great Ormond Street Hospital), Amal Al-Seraihy(King Faisal Specialist Hospital & Research Centre), Etai Adam(University of Southern California), Matthias Felber, Barış Malbora(Istanbul Yeni Yüzyıl University), Mohammed Essa(King Abdulaziz Medical City), Srividhya Senthil(Manchester University NHS Foundation Trust), Rakefet Sidlik Muskatel(Schneider Children's Medical Center), Mayada Abu Shanap(King Hussein Cancer Center), Jacek Winiarski(Karolinska University Hospital), Michael H. Albert(LMU Klinikum), Marta González‐Vicent(Hospital Infantil Universitario Niño Jesús), Melek Erdem(Altınbaş University), Serap Aksoylar(Ege University), Hawazen Saleh Alsaedi(King Faisal Specialist Hospital & Research Centre), M. Akif Yeşilipek(Akdeniz University), Nuno Miranda(IPO Porto), Marco Zecca(Policlinico San Matteo Fondazione), Barış Kuşkonmaz(Hacettepe University), Zohreh Nademi(Great North Children's Hospital), Maura Faraci(Istituto Giannina Gaslini), Jean‐Sébastien Diana(Délégation Paris 5), Martin Castelle(Hôpital Necker-Enfants Malades), Amir Ali Hamidieh(Stem Cell Technology Research Center), Alphan Küpesiz(Akdeniz University), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Beki James(Leeds Teaching Hospitals NHS Trust), Kerstin Felgentreff(University Hospital Ulm), Sophie Van Lancker(Ghent University Hospital), Musa Karakükçü(Erciyes University), Robert Wynn(Royal Manchester Children's Hospital), Marleen Renard(Universitair Ziekenhuis Leuven), Renata Formánková(Charles University), Jeroen Knippenberg(European Society for Blood and Marrow Transplantation), Sarah Lawson(Boston Children's Hospital), Natalia Maximova(IRCCS Materno Infantile Burlo Garofolo), Irina Zaidman(Hebrew University of Jerusalem), Franco Locatelli(University of Pavia), Patrick Gilbert, Bénedicte Bruno(Centre Hospitalier Universitaire de Lille), Ingrid Furlan(University of Freiburg), Juliana Silva(Great Ormond Street Hospital), Robbert Bredius(Leiden University Medical Center), K. Suresh Rao(Great Ormond Street Hospital), Т А Быкова(First Pavlov State Medical University of St. Petersburg), Persis Amrolia(Great Ormond Street Hospital), C. Rénard(Institut d’Hématologie et d’Oncologie Pédiatrique), Tariq Ghafoor, Catherine Paillard(Sorbonne Université)
Blood
November 3, 2025
Cited by 3


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