Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study
Federica Barzaghi(The San Raffaele Telethon Institute for Gene Therapy), Rakesh K. Goyal(Children's Hospital of Pittsburgh), Bénédicte Neven(Université Paris-Panthéon-Assas), Marina Cavazzana(Université Rennes 2), Safa Barış(Marmara University), Sandra Steinmann, Ansgar Schulz(University Hospital Ulm), Caridad Martinez(Baylor College of Medicine), O Marie(Hôpital Necker-Enfants Malades), Despina Moshous(Hôpital Necker-Enfants Malades), Elif Karakoç-Aydıner(Marmara University), Hirokazu Kanegane(Tokyo Medical and Dental University), Jong Jin Seo(Ulsan College), Michael H. Albert(LMU Klinikum), Ayça Kıykım(Marmara University), Marta González‐Vicent(Hospital Infantil Universitario Niño Jesús), Luis Murguía-Favela(Hospital for Sick Children), William T. Shearer(Baylor College of Medicine), Juliana Folloni Fernandes(Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo), Frank M. Ruemmele(Délégation Paris 5), Waseem Qasim(University College London), Anna Roppelt, Zohreh Nademi(Great North Children's Hospital), Ánita Lawitschka(St Anna Children's Hospital), Alessandro Aiuti(University of Rome Tor Vergata), Austen Worth(Great Ormond Street Hospital), Cristina Díaz de Heredia(Hospital Materno-Infantil), Eleonora Gambineri(Meyer Children's Hospital), Jack Bleesing(Cincinnati Children's Hospital Medical Center), Erlinda R. Ulloa(University of California, Irvine), Lucia Dora Notarangelo(Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia), Mary Slatter(First Pavlov State Medical University of St. Petersburg), Côme Tissandier(Délégation Paris 5), Ahmet Özen(Fakultet za Poslovni Menadžment u Baru), Frédéric Rieux‐Laucat(Inserm), Magda Carneiro‐Sampaio(Universidade de São Paulo), Ichiro Kobayashi(NTT Medical Center), Barbarella Lucarelli(University of Pavia), Miguel Ángel Díaz(Hospital Infantil Universitario Niño Jesús), Laura Alonso(Vall d'Hebron Hospital Universitari), Anna Shcherbina, Zeynep Yesim Kucuk(Cincinnati Children's Hospital Medical Center), Silvia Ricci(Meyer Children's Hospital), Stéphane Blanche(Délégation Paris 5), Alain Fisher(Délégation Paris 5), Lisa R. Forbes(Baylor College of Medicine), Carsten Speckmann(University of Freiburg), Juliana Silva(Great Ormond Street Hospital), Paolo Lionetti(Meyer Children's Hospital)
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