Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study
Federica Barzaghi(The San Raffaele Telethon Institute for Gene Therapy), Laura Cristina Amaya Hernandez(Stanford University), Bénédicte Neven(Délégation Paris 5), Silvia Ricci(Meyer Children's Hospital), Zeynep Yesim Kucuk(Cincinnati Children's Hospital Medical Center), Jack Bleesing(Cincinnati Children's Hospital Medical Center), Zohreh Nademi(Great North Children's Hospital), Mary Slatter(Great North Children's Hospital), Erlinda R. Ulloa(Boston Children's Hospital), Anna Shcherbina, Anna Roppelt, Austen Worth(Great Ormond Street Hospital), Juliana Silva(Great Ormond Street Hospital), Alessandro Aiuti(Vita-Salute San Raffaele University), Luis Murguía-Favela(Hospital for Sick Children), Carsten Speckmann(University of Freiburg), Magda Carneiro‐Sampaio(Universidade de São Paulo), Juliana Folloni Fernandes(Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo), Safa Barış(Marmara University), Ahmet Özen(Marmara University), Elif Karakoç-Aydıner(Marmara University), Ayça Kıykım(Marmara University), Ansgar Schulz, Sandra Steinmann, Lucia Dora Notarangelo(Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia), Eleonora Gambineri(Meyer Children's Hospital), Paolo Lionetti(Meyer Children's Hospital), William T. Shearer(Baylor College of Medicine), Lisa R. Forbes(Baylor College of Medicine), Caridad Martinez(Baylor College of Medicine), Despina Moshous(Délégation Paris 5), Stéphane Blanche(Délégation Paris 5), Alain Fisher(Délégation Paris 5), Frank M. Ruemmele(Délégation Paris 5), Côme Tissandier(Délégation Paris 5), O Marie(Assistance Publique – Hôpitaux de Paris), Frédéric Rieux‐Laucat(Inserm), Marina Cavazzana(Délégation Paris 5), Waseem Qasim(Great Ormond Street Hospital), Barbarella Lucarelli(University of Pavia), Michael H. Albert(Ludwig-Maximilians-Universität München), Ichiro Kobayashi(NTT Medical Center), Laura Alonso(Vall d'Hebron Hospital Universitari), Cristina Díaz de Heredia(Vall d'Hebron Hospital Universitari), Hirokazu Kanegane(Tokyo Medical and Dental University), Ánita Lawitschka(St Anna Children's Hospital), Jong Jin Seo(Ulsan College), Marta González‐Vicent(Hospital Infantil Universitario Niño Jesús), Miguel Ángel Díaz(Hospital Infantil Universitario Niño Jesús), Rakesh K. Goyal(Children's Hospital of Pittsburgh), Martin G. Sauer(Medizinische Hochschule Hannover), Akif Yeşilipek(Antalya IVF), Min‐Soo Kim(Columbia University Irving Medical Center), Yeşim Yılmaz Demirdağ(Columbia University Irving Medical Center), Monica Bhatia(Columbia University Irving Medical Center), Julie Khlevner(Columbia University Irving Medical Center), Erick J. Richmond Padilla, Silvana Martino(Ospedale Regina Margherita), Davide Montin(Ospedale Regina Margherita), Olaf Neth(Instituto de Biomedicina de Sevilla), Águeda Molinos-Quintana(Instituto de Biomedicina de Sevilla), Justo Valverde-Fernández(Consejo Superior de Investigaciones Científicas), Arnon Broides(Ben-Gurion University of the Negev), Vered Pinsk(Ben-Gurion University of the Negev), Antje Ballauf(Helios Klinikum Krefeld), Filomeen Haerynck(Ghent University Hospital), Victoria Bordon(Ghent University Hospital), Catharina Dhooge(Ghent University Hospital), Maria Garcia-Lloret(University of California, Los Angeles), Robbert G. M. Bredius(Leiden University Medical Center), Krzysztof Kałwak(Wroclaw Medical University), Élie Haddad(Université de Montréal), Markus G. Seidel(Medical University of Graz), Gregor Dückers(Helios Klinikum Krefeld), Sung‐Yun Pai(Boston Children's Hospital), Christopher C. Dvorak(University of California, San Francisco), Stephan Ehl(University of Freiburg), Franco Locatelli(University of Pavia), Frederick D. Goldman(University of Alabama at Birmingham), Andrew R. Gennery(Great North Children's Hospital), Mort J. Cowan(University of California, San Francisco), Maria-Grazia Roncarolo(Stanford University), Rosa Bacchetta(Stanford Medicine)
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