Efficacy of mitapivat in patients with transfusion-dependent alpha-thalassemia: Subgroup analysis from the ENERGIZE-T trial

Ashutosh Lal(Post Graduate Institute of Medical Education and Research), Vip Viprakasit(Siriraj Hospital), Hui Shao(University of Louisville), Noppacharn Uaprasert(Chulalongkorn University), Ferras Alashkar(Essen University Hospital), Sujit Sheth(Columbia University Irving Medical Center), Lauren Czapla(Agios Pharmaceuticals (United States)), Antonis Kattamis, Khaled M. Musallam(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Maria Domenica Cappellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Kevin H.M. Kuo(University Health Network), Keely Gilroy(Agios Pharmaceuticals (United States)), Hanny Al‐Samkari(Harvard University), Manuela Balocco(Ospedale Microcitemico), Anita W. Rijneveld(Erasmus MC Cancer Institute), Bart J. Biemond(Amsterdam University Medical Centers), Alì Taher(American University of Beirut Medical Center), Efthymia Vlachaki(Senologic Hellenic Society), Andreas Glenthøj(University of Copenhagen), Nattiya Teawtrakul(Khon Kaen University), Adisak Tantiworawit(Ente Ospedaliero Ospedali Galliera), Jeremie H. Estepp(St. Jude Children's Research Hospital)
Blood
November 3, 2025
Cited by 2


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