A Phase 3 Trial of Luspatercept in Patients with Transfusion-Dependent β-Thalassemia

Maria Domenica Cappellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Antonio Piga(University of Turin), Ashutosh Lal(Post Graduate Institute of Medical Education and Research), Raffaella Origa(Ospedale Microcitemico), P. Joy Ho(The University of Sydney), Ellis J. Neufeld(St. Jude Children's Research Hospital), Liana Gercheva(National Institute of Emergency Medicine "Pirogov"), Ersi Voskaridou(Laiko General Hospital of Athens), Penka Ganeva(Ente Ospedaliero Ospedali Galliera), Soo-min Lim(Kyungpook National University), Yeşim Aydınok(Ente Ospedaliero Ospedali Galliera), Tatiana Zinger(Incyte (United States)), Abderrahim Khélif(Ente Ospedaliero Ospedali Galliera), Alexis A. Thompson(Children's Hospital of Philadelphia), Farrukh Shah(Ente Ospedaliero Ospedali Galliera), Silverio Perrotta(University Hospital Foundation), John B. Porter(Royal London Hospital), Jeevan K. Shetty(Ente Ospedaliero Ospedali Galliera), Pencho Georgiev(University Multipurpose Hospital for Active Treatment "Sveti Georgi"), Antonis Kattamis, Jennie Zhang(Bristol-Myers Squibb (United States)), Abderrahmane Laadem(Daiichi Sankyo (India)), Kevin H.M. Kuo(University Health Network), Olivier Hermine(Centre National de la Recherche Scientifique), Jun Zou(Fudan University), Hong-Keng Liew(Ente Ospedaliero Ospedali Galliera), Alì Taher(American University of Beirut Medical Center), Thomas D. Coates(Children's Hospital of Los Angeles), Idit Pazgal-Kobrowski(Rabin Medical Center), Vip Viprakasit(Siriraj Hospital), Lee-Ping Chew(Sarawak General Hospital), Matthew L. Sherman, Ping Chong Bee(University Malaya Medical Centre), Dimana Miteva(Bristol-Myers Squibb (Switzerland)), Efthymia Vlachaki(Senologic Hellenic Society), Adisak Tantiworawit(Ente Ospedaliero Ospedali Galliera), Mohamed Béjaoui(Tunis University), Peter G. Linde(Ente Ospedaliero Ospedali Galliera), Meng‐Yao Lu(National Taiwan University Hospital)
New England Journal of Medicine
March 25, 2020
Cited by 320


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