Patient journey to Fabry disease diagnosis in the United States: an observational retrospective analysis of two United States claims databases

Alexandra Dumitriu(Sanofi (United States)), Natalia Petruski‐Ivleva(AVEO Oncology (United States)), Michael B. Jordan(Cincinnati Children's Hospital Medical Center), Claudia Leiras, Ana Maria Viegas-Crespo(Sanofi (United States)), Tiange Yu, Queeny Ip, И. А. Максимова(Lomonosov Moscow State University), Roberto Araujo, Gandarvaka Miles
Orphanet Journal of Rare Diseases
November 27, 2025
Cited by 0


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