Allogeneic hematopoietic cell transplantation for XIAP deficiency: an international survey reveals poor outcomes
Rebecca Marsh(Cincinnati Children's Hospital Medical Center), Alexandra H. Filipovich(Carolinas Medical Center), Alain Fischer(Inserm), Hirokazu Kanegane(Tokyo Medical and Dental University), James T. Casper(Children's Hospital of Wisconsin), Michael B. Jordan(Cincinnati Children's Hospital Medical Center), Prakash Satwani(Pediatrics and Genetics), Vincent Barlogis, Kai Lehmberg(Universität Hamburg), Paul Veys(Great Ormond Street Hospital), Jack Bleesing(Cincinnati Children's Hospital Medical Center), Sam Milanovich(Children's Hospital of Wisconsin), Persis Amrolia(Great Ormond Street Hospital), Dorothea Douglas(University of Arizona), Sylvain Latour(Institut des Maladies Génétiques Imagine), Kazuko Hamamoto(Japanese Red Cross Hiroshima College of Nursing), Dandan Li(China University of Geosciences (Beijing)), Mi‐Ok Kim(Bristol-Myers Squibb (United States)), Ashish Kumar(King's College London), Petr Sedláček(University Hospital in Motol), David A. Margolis(Medical College of Wisconsin), Ingo Müller(Universität Hamburg), Kanchan Rao(Great Ormond Street Hospital), David Dimmock(Children’s Institute)
Cited by 144
Related Papers
<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1
|Science|2003|3.5k
Impaired type I interferon activity and inflammatory responses in severe COVID-19 patients
|Science|2020|3.2k
Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
|Science|2000|2.6k
A Serious Adverse Event after Successful Gene Therapy for X-Linked Severe Combined Immunodeficiency
|New England Journal of Medicine|2003|1.8k
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
|Journal of Clinical Investigation|2008|1.8k