Hematopoietic stem cell transplantation for purine nucleoside phosphorylase deficiency: an EBMT-IEWP retrospective study

U. Herrmann(University of Bern), Tayfun Güngör, Alexandra Laberko(Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology), Bénédicte Neven(Université Paris-Panthéon-Assas), Matthias Felber, Aydan İkincioğulları(Ankara University), Michael S. Hershfield(Duke University), Andrew R. Gennery(Newcastle upon Tyne Hospitals NHS Foundation Trust), Mary Coussons(Royal Manchester Children's Hospital), Ansgar Schulz(University Hospital Ulm), Fabian Hauck(Ludwig-Maximilians-Universität München), Robbert G. M. Bredius(Leiden University Medical Center), Michael H. Albert(LMU Klinikum), Andreas H. Groll(University Hospital Münster), Figen Doğu(Ankara University), Brigitte Strahm(University Medical Center Freiburg), Isabelle Meyts(KU Leuven), Zehra Şule Haskoloğlu(Ankara University), M. Akif Yeşilipek(Akdeniz University), Caroline A. Lindemans(University Medical Center Utrecht), Victor Lewis(Alberta Children's Hospital), Felix Zirngibl(Humboldt-Universität zu Berlin), Austen Worth(Great Ormond Street Hospital), Annette Hackenberg(University of Zurich), Arjan C. Lankester(Leiden University Medical Center), Robert Wynn(Royal Manchester Children's Hospital), Gregory M.T. Guilcher(University of Calgary), Ulrike Zeilhofer(University Children's Hospital Zurich), Claudia Bettoni da Cunha Riehm(Medizinische Hochschule Hannover), Irina Zaidman(Hebrew University of Jerusalem), Patrick Gilbert, Mirjam Völler(Humboldt-Universität zu Berlin), E. Graham Davies(Great Ormond Street Hospital), Suhag Parikh(Emory University), Manfred Hönig(Universität Ulm), Mathias Hauri‐Hohl(University Children's Hospital Zurich)
Blood
September 22, 2025
Cited by 2


Related Papers