Therapeutic genetic restoration through allogeneic brain microglia replacement
Marius Marc-Daniel Mader(Stanford University), Marius Wernig(California Institute for Regenerative Medicine), Alexa Scavetti(Stanford University), Takeshi Uenaka(Stanford University), Aaron Tianyue Chai(California Institute for Regenerative Medicine), Yongjin Yoo(California Institute for Regenerative Medicine)
Cited by 21
Related Papers
In Situ Genetic Correction of the Sickle Cell Anemia Mutation in Human Induced Pluripotent Stem Cells Using Engineered Zinc Finger Nucleases
|Stem Cells|2011|311
Telomere shortening and loss of self-renewal in dyskeratosis congenita induced pluripotent stem cells
|Nature|2011|260
AMPA receptor GluA2 subunit defects are a cause of neurodevelopmental disorders
|Nature Communications|2019|248