In Situ Genetic Correction of the Sickle Cell Anemia Mutation in Human Induced Pluripotent Stem Cells Using Engineered Zinc Finger Nucleases

Vittorio Sebastiano(California Institute for Regenerative Medicine), J. Keith Joung(Massachusetts General Hospital), Dana T. Yeo(Stanford University), Bahareh Haddad(Stanford University), James Angstman(Massachusetts General Hospital), Steven E. Artandi(Stanford University), Luís F.Z. Batista(Washington University in St. Louis), John S. Hawkins(Stanford University), Cherie L. Ramirez(Harvard University), Cyd Khayter(Massachusetts General Hospital), Morgan L. Maeder(Editas Medicine (United States)), Marius Wernig(Stanford University), Mathew J. Goodwin(Massachusetts General Hospital)
Stem Cells
September 2, 2011
10.1002/stem.718
Cited by 311

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