Limb-Girdle Muscular Dystrophy Scientific Workshop
Matthew Wicklund(The University of Texas at San Antonio Health Science Center), Kim Bryant(Foundation for Excellence in Education), Douglas M. Sproule(BridgeBio (United States)), Nicholas E. Johnson(Virginia Commonwealth University), Lindsay N. Alfano(Nationwide Children's Hospital), Katherine D. Mathews(University of Iowa), Peter B. Kang(Boston Children's Hospital), Nicole Verdun(Center for Biologics Evaluation and Research), Peter Marks(Johns Hopkins University), Jerry R. Mendell(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Sarepta Therapeutics (United States))
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