Key lessons from the first international treatment eligibility committee: the case of metachromatic leukodystrophy
Daphne H. Schoenmakers(Amsterdam Neuroscience), Nicole I. Wolf(Emma Kinderziekenhuis), Laura Adang(Children's Hospital of Philadelphia), Roswitha Lüftinger(St Anna Children's Hospital), Mareen R. Datema(Amsterdam UMC Location University of Amsterdam), Sabine Grønborg(Copenhagen University Hospital), Herbert Pichler(St Anna Children's Hospital), Klára Brožová(Charles University), Tom J. de Koning(University Medical Center Utrecht), Carla E. M. Hollak(Centre For Development Studies), Valeria Calbi(IRCCS Ospedale San Raffaele), Caroline G. Bergner(Leipzig University), Fanny Mochel(Inserm), Johanna Uusimaa(Oulu University Hospital), Ángeles García‐Cazorla(Hospital Sant Joan de Déu Barcelona), Lucia Laugwitz(University Children's Hospital Tübingen), Caroline A. Lindemans(University Medical Center Utrecht), Caroline Sevin(Bicêtre Hospital), Tamara J. Martin(University Children's Hospital Tübingen), Alejandra Darling(Hospital Sant Joan de Déu Barcelona), Samuel Groeschel(University of Tübingen), Erik A. Eklund(Lund University), Peter M. van Hasselt(Utrecht University), Morten Andreas Horn(Oslo University Hospital), Ayelet Zerem(Tel Aviv University), Hanka Dekker(Netherlands Metabolomics Centre), Lüdger Schöls(German Center for Neurodegenerative Diseases), Annette Bley(Kinderkrebs-Zentrum Hamburg), Holm Graeßner(University Children's Hospital Tübingen), Dipak Ram(Royal Manchester Children's Hospital), Päivi Vieira(Oulu University Hospital), Francesca Fumagalli(Vita-Salute San Raffaele University), Michal Inbar‐Feigenberg(University of Toronto), Christiane Kehrer(University Children's Hospital Tübingen), Andreas Øberg(Oslo University Hospital), Jaap Jan Boelens(Wilhelmina Children's Hospital), Marije A B C Asbreuk(Amsterdam Neuroscience), Shanice Beerepoot(Amsterdam Neuroscience)
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