Optimized Prime Editing of Human Induced Pluripotent Stem Cells to Efficiently Generate Isogenic Models of Mendelian Diseases

Rodrigo Cerna-Chavez(Massachusetts Eye and Ear Infirmary), Marcela Garita‐Hernandez(Centre National de la Recherche Scientifique), Alba Ortega-Gascó(Instituto de Salud Carlos III), Eric A. Pierce(Broad Institute), Thibaud Metais(Massachusetts Eye and Ear Infirmary), Michael J. Scandura(Massachusetts Eye and Ear Infirmary), Kinga M. Bujakowska(Massachusetts Eye and Ear Infirmary), Nathan Ehrenreich(Massachusetts Eye and Ear Infirmary), Hafiz Muhammad Azhar Baig(Massachusetts Eye and Ear Infirmary)
International Journal of Molecular Sciences
December 26, 2024
Cited by 6


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