Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration
Francesca Simonelli(University of Campania "Luigi Vanvitelli"), Albert M. Maguire(Children's Hospital of Philadelphia), Francesco Testa(University of Campania "Luigi Vanvitelli"), Eric A. Pierce(Penn Presbyterian Medical Center), Federico Mingozzi(Children's Hospital of Philadelphia), Jeannette Bennicelli(Penn Presbyterian Medical Center), Settimio Rossi(University of Campania "Luigi Vanvitelli"), Kathleen Marshall(Children's Hospital of Philadelphia), Sandro Banfi(Telethon Institute Of Genetics And Medicine), Enrico Maria Surace(Telethon Institute Of Genetics And Medicine), Junwei Sun(Children's Hospital of Philadelphia), T. Michael Redmond(National Eye Institute), Xiaosong Zhu(Children's Hospital of Philadelphia), Kenneth S. Shindler(Penn Presbyterian Medical Center), Gui‐Shuang Ying(Penn Presbyterian Medical Center), Carmela Ziviello(Institute of Genetics and Biophysics), Carmela Acerra(Children's Hospital of Philadelphia), J. Fraser Wright(Children's Hospital of Philadelphia), Jennifer Wellman McDonnell(Children's Hospital of Philadelphia), Katherine A. High(Children's Hospital of Philadelphia), Jean Bennett(Children's Hospital of Philadelphia), Alberto Auricchio(Telethon Institute Of Genetics And Medicine)
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