Gene therapy in advanced metachromatic leukodystrophy: tempering expectations
Daphne H. Schoenmakers(Amsterdam Neuroscience), Francesca Fumagalli(Vita-Salute San Raffaele University), Laura Adang(Children's Hospital of Philadelphia), Sabine Grønborg(Copenhagen University Hospital), Nicole I. Wolf(Emma Kinderziekenhuis), Ángeles García Cazorla(Hospital Sant Joan de Déu Barcelona), Carla E. M. Hollak(Centre For Development Studies), Pascal Martin(Hertie Institute for Clinical Brain Research), Valeria Calbi(IRCCS Ospedale San Raffaele), Caroline G. Bergner(Leipzig University), Fanny Mochel(Inserm), Lucia Laugwitz(University Children's Hospital Tübingen), Caroline A. Lindemans(University Medical Center Utrecht), Caroline Sevin(Bicêtre Hospital), Simon Jones(Manchester University NHS Foundation Trust), Alejandra Darling(Hospital Sant Joan de Déu Barcelona), Samuel Groeschel(University of Tübingen), Claire Horgan(Manchester University NHS Foundation Trust), Erik A. Eklund(Lund University), Peter M. van Hasselt(Utrecht University), Ayelet Zerem(Tel Aviv University), Lüdger Schöls(German Center for Neurodegenerative Diseases), Annette Bley(Kinderkrebs-Zentrum Hamburg), Dipak Ram(Royal Manchester Children's Hospital), Andreas Øberg(Oslo University Hospital), Tom de Koning(Lund University), Jaap Jan Boelens(Wilhelmina Children's Hospital), Marije A B C Asbreuk(Amsterdam Neuroscience), Shanice Beerepoot(Amsterdam Neuroscience)
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