322P Rasch evaluation of North Star Ambulatory Assessment and North Star Assessment for limb-girdle type muscular dystrophies in Becker muscular dystrophy
L. Lowes(Nationwide Children's Hospital), James E. MacDougall(BioBridges (United States)), L. Alfano(Nationwide Children's Hospital), Michelle Eagle(Newcastle University), J. Vissing(University of Copenhagen), Michelle A. James(Shriners Hospitals for Children - Erie), H. Phan(Rare Disease Therapeutics (United States)), C. McDonald, J. Donovan, Anna Mayhew(Newcastle upon Tyne Hospitals NHS Foundation Trust)
Cited by 1
Related Papers
A phase I/IItrial of MYO‐029 in adult subjects with muscular dystrophy
|Annals of Neurology|2008|466
Caveolin 1 Is Overexpressed and Amplified in a Subset of Basal-like and Metaplastic Breast Carcinomas: A Morphologic, Ultrastructural, Immunohistochemical, and <i>In situ</i> Hybridization Analysis
|Clinical Cancer Research|2007|208
Muscle MRI in patients with dysferlinopathy: pattern recognition and implications for clinical trials
|Journal of Neurology Neurosurgery & Psychiatry|2018|118
Newborn screening for spinal muscular atrophy: Anticipating an imminent need
|Seminars in Perinatology|2015|79