Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy
Amel Karaa(Istituto delle Scienze Neurologiche di Bologna), Engelstad Kristin, Gráinne S. Gorman(Wellcome Centre for Mitochondrial Research), Bruce H. Cohen(Akron Children's Hospital), Gregory M. Enns(Lucile Packard Children's Hospital), Jeffrey S. Finman(Jupiter Medical Center), Gessica Vasco(Bambino Gesù Children's Hospital), Fernando Scaglia(Baylor College of Medicine), Amy B. Goldstein(Northwell Health), Mark A. Tarnopolsky(McMaster University), Mary Kay Koenig, Jerry Vockley(Pittsburgh Public Schools), Serenella Servidei(Università Cattolica del Sacro Cuore), Thomas Klopstock(Ludwig-Maximilians-Universität München), Cornelia Kornblum(University of Bonn), Sumit Parikh(Cleveland Clinic), Anna Lehman(University of British Columbia), A. Noelle Larson(Mayo Clinic), Russell P. Saneto(Seattle Children's Hospital), Costanza Lamperti(West Virginia University), Marni J. Falk(Children's Hospital of Philadelphia), Enrico Bertini(Bambino Gesù Children's Hospital), Valério Carelli(Istituto delle Scienze Neurologiche di Bologna), Daria Diodato(Bambino Gesù Children's Hospital), Johan L.K. Van Hove(Children's Hospital Colorado), Mária Judit Molnár(Istituto delle Scienze Neurologiche di Bologna), Enrico Bugiardini, António Toscano(University of Messina), David A. Brown(Istituto delle Scienze Neurologiche di Bologna), James A. Shiffer(Istituto delle Scienze Neurologiche di Bologna), Valentino Maria Lucia, Poole Olivia, Nithi Ajantha, Kendall Fran, Grosz Zoltan, Györgyi Bathori, Soler-Alfonso Claudia, Nicola Longo(Center for Human Genetics), Hanna Michael G, Michio Hirano(Columbia University Irving Medical Center), Michelango Mancuso(Istituto delle Scienze Neurologiche di Bologna), H. Phan(Rare Disease Therapeutics (United States)), Abdullhameed May Ali, Sancricca Cristina, Richard Haas(University of California San Diego), John Vissing(University of Copenhagen), P. Alessandro, Robert D. S. Pitceathly(National Hospital for Neurology and Neurosurgery)
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