Intrathecal Gene Therapy for Giant Axonal Neuropathy
Diana Bharucha‐Goebel(National Institutes of Health), Carsten G. Bönnemann(National Institute of Neurological Disorders and Stroke), Wadih M. Zein(Johns Hopkins University), Bradley P. Carlin(University of Minnesota), Minal Jain(Johns Hopkins University), Thomas O. Crawford(Johns Hopkins University), Denis Rybin(Boston University), Ahmet Höke(Johns Hopkins University), Tanya Lehky(National Institutes of Health), Diane Armao, Lawrence Charnas(Johns Hopkins University), Roberto Calcedo(Johns Hopkins University), Laryssa A. Huryn(Johns Hopkins University), John D. Heiss(National Institutes of Health), Jody E. Hooper(Johns Hopkins University), Payam Mohassel(Johns Hopkins University), Joshua J. Todd(Vanderbilt University), Thomas W. Bouldin(University of North Carolina at Chapel Hill), Jessica A. Chichester(Johns Hopkins University), A. Reghan Foley(National Institutes of Health), Rachel M. Bailey(Johns Hopkins University), Dimah Saade(University of Iowa), Elizabeth M. Kang(National Institute of Allergy and Infectious Diseases), Beth Seremula(Johns Hopkins University), Steven J. Gray(Johns Hopkins University), Charlotte J. Sumner(Johns Hopkins University), Eshetu Tesfaye(Johns Hopkins University), M. Waite(Johns Hopkins University), Gina Norato(Johns Hopkins University)
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