Intrathecal Gene Therapy for Giant Axonal Neuropathy
Diana Bharucha‐Goebel(National Institutes of Health), Carsten G. Bönnemann(National Institutes of Health), Wadih M. Zein(Johns Hopkins University), Bradley P. Carlin(Johns Hopkins University), Minal Jain(Johns Hopkins University), Thomas O. Crawford(Johns Hopkins University), Denis Rybin(Boston University), Ahmet Höke(Johns Hopkins University), Tanya Lehky(National Institutes of Health), Diane Armao, Lawrence Charnas(Johns Hopkins University), Roberto Calcedo(Johns Hopkins University), Laryssa A. Huryn(Johns Hopkins University), John D. Heiss(National Institutes of Health), Jody E. Hooper(Johns Hopkins University), Payam Mohassel(National Institutes of Health), Joshua J. Todd(Vanderbilt University), Thomas W. Bouldin(University of North Carolina at Chapel Hill), Jessica A. Chichester(Johns Hopkins University), A. Reghan Foley(National Institutes of Health), Rachel M. Bailey(Johns Hopkins University), Dimah Saade(University of Iowa), Elizabeth M. Kang(National Institute of Allergy and Infectious Diseases), Beth Seremula(Johns Hopkins University), Steven J. Gray(Johns Hopkins University), Charlotte J. Sumner(Johns Hopkins University), Eshetu Tesfaye(Johns Hopkins University), M. Waite(Johns Hopkins University), Gina Norato(Johns Hopkins University)
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