Mitapivat improves ineffective erythropoiesis and iron overload in adult patients with pyruvate kinase deficiency
Eduard J. van Beers(Utrecht University), Kevin H.M. Kuo(University Health Network), Rachael F. Grace(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Vanessa Beynon(Agios Pharmaceuticals (United States)), Wilma Barcellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Melissa L. DiBacco(Agios Pharmaceuticals (United States)), John B. Porter(Royal London Hospital), Parija Patel(Agios Pharmaceuticals (United States)), Hanny Al‐Samkari(Harvard University), Andreas Glenthøj(University of Copenhagen), Megan Wind‐Rotolo(Bristol-Myers Squibb (United States)), Rengyi Xu(Agios Pharmaceuticals (United States))
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