P255 Effects of EDG-5506, a fast myosin modulator, on function and biomarkers of muscle damage in adults with Becker muscular dystrophy (BMD)
Sarah Collins, J. Donovan(Healthwise), Maria Mancini(Champions Oncology (United States)), Alan J. Russell(Healthwise), H. Phan(Rare Disease Therapeutics (United States)), L. Thaler(Emory University), James E. MacDougall(BioBridges (United States)), B. Barthel(Healthwise), N. Kilburn
Cited by 1
Related Papers
Hyperglycemia: An Independent Marker of In-Hospital Mortality in Patients with Undiagnosed Diabetes
|The Journal of Clinical Endocrinology & Metabolism|2002|2.1k
Newborn screening for spinal muscular atrophy: Anticipating an imminent need
|Seminars in Perinatology|2015|79
Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy
|Neurology|2023|74
The Survival of Motor Neuron Protein Acts as a Molecular Chaperone for mRNP Assembly
|Cell Reports|2017|71
Sleep profiles in children with down syndrome
|American Journal of Medical Genetics Part A|2015|53