P1497: MITAPIVAT IMPROVES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE REGULARLY TRANSFUSED

Eduard J. van Beers(Utrecht University), Kevin H.M. Kuo(University Health Network), Rachael F. Grace(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Vanessa Beynon(Agios Pharmaceuticals (United States)), Wilma Barcellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), John B. Porter(Royal London Hospital), Parija Patel(Agios Pharmaceuticals (United States)), Melissa Dibacco(Agios Pharmaceuticals (United States)), Hanny Al‐Samkari(Harvard University), Andreas Glenthøj(University of Copenhagen), Megan Wind‐Rotolo(Bristol-Myers Squibb (United States)), Rengyi Xu(Agios Pharmaceuticals (United States))
HemaSphere
August 1, 2023
Cited by 1


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