Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

Monica S. Thakar(Fred Hutch Cancer Center), Michael D. Keller(Children's National), Roberta Parrott(Duke University), Evan Shereck(Oregon Health & Science University), Kathleen E. Sullivan(University of Pennsylvania), Ahmad Rayes(Cincinnati Children's Hospital Medical Center), Mark T. Vander Lugt(University of Michigan–Ann Arbor), Geoff D.E. Cuvelier(CancerCare Manitoba), Jeffrey R. Andolina(Golisano Children's Hospital), Lisa Forbes Satter(Baylor College of Medicine), Jennifer M. Puck(University of California, San Francisco), Sung‐Yun Pai(Dana-Farber Cancer Institute), Alan P. Knutsen(St. Louis Children's Hospital), Frederick D. Goldman(University of Alabama at Birmingham), Pierre Teira(Université de Montréal), Brent R. Logan(Cape Town HVTN Immunology Laboratory / Hutchinson Centre Research Institute of South Africa), Caridad Martinez(Baylor College of Medicine), Alfred P. Gillio(University Medical Center), Emi Caywood(Alfred I. duPont Hospital for Children), Shanmuganathan Chandrakasan(Emory University), Christen L. Ebens(University of Minnesota), Hesham Eissa(Children's Hospital Colorado), Blachy J. Dávila Saldaña(Children's National), Jennifer Heimall(Children's Hospital of Philadelphia), Susan E. Prockop(Memorial Sloan Kettering Cancer Center), Morton J. Cowan(Blood Systems Research Institute), Olatundun Williams(Columbia University), Theodore B. Moore(University of California, Los Angeles), Lolie C. Yu(Louisiana State University), Malika Kapadia(Harvard University), Jack Bleesing(Cincinnati Children's Hospital Medical Center), Ami J. Shah(University of California, Los Angeles), Kenneth B. DeSantes(University of Wisconsin–Madison), Jeffrey J. Bednarski(Washington University in St. Louis), Sonali Chaudhury(Northwestern University), Sharat Chandra(Cincinnati Children's Hospital Medical Center), Soma Jyonouchi(Children's Hospital of Philadelphia), Jasmeen Dara(University of California, San Francisco), Lauri M. Burroughs(Fred Hutch Cancer Center), Lisa Madden(CHRISTUS Transplant Institute), Larisa Broglie(Morgan Stanley Children's Hospital), Rebecca H. Buckley(Duke Medical Center), Neena Kapoor(University of Southern California), Xuerong Liu(Medical College of Wisconsin), Aleksandra Petrović(Seattle Children's Hospital), Richard J. O’Reilly(Memorial Sloan Kettering Cancer Center), Victor M. Aquino(The University of Texas Southwestern Medical Center), Jacob Rozmus(University of British Columbia), Elizabeth Dunn(Midland Regional Hospital Mullingar), Deepak Chellapandian(Johns Hopkins University)
The Lancet
June 20, 2023
Cited by 123


Related Papers