Phase 3 trial of defibrotide for the treatment of severe veno-occlusive disease and multi-organ failurePaul G. Richardson, Robert J. Soiffer, Marcie Riches et al.|Blood|2016Cited by 333
Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC reportLauri M. Burroughs, Sung‐Yun Pai, Aleksandra Petrović et al.|Blood|2020Cited by 142
Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathiesAllison A. King, Shalini Shenoy, Naynesh Kamani et al.|American Journal of Hematology|2015Cited by 131
Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment ConsortiumMonica S. Thakar, Michael D. Keller, Brent R. Logan et al.|The Lancet|2023Cited by 123
The genetic landscape of severe combined immunodeficiency in the United States and Canada in the current era (2010-2018)Christopher C. Dvorak, Jennifer M. Puck, Élie Haddad et al.|Journal of Allergy and Clinical Immunology|2018Cited by 85