Base editing strategies to convert CAG to CAA diminish the disease-causing mutation in Huntington's disease
Doo Eun Choi(Harvard University), Jong‐Min Lee(Broad Institute), Vanessa C. Wheeler(Harvard University), Jae-Hyun Jang(Harvard University), Benjamin P. Kleinstiver(Harvard University), Hannah E. Stutzman(Massachusetts General Hospital), Sophia Zeng(Massachusetts General Hospital), Jun Wan Shin(Harvard University), Jacob M. Loupe, Eun Pyo Hong
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