The Pyruvate Kinase Deficiency Global Longitudinal (Peak) Registry: rationale and study design
Rachael F. Grace(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Paola Bianchi(University of Pavia), Bertil Glader(Stanford University), Chris Bowden(Agios Pharmaceuticals (United States)), Joan‐Lluís Vives Corrons(Josep Carreras Leukaemia Research Institute), Kevin H.M. Kuo(University Health Network), Vip Viprakasit(Siriraj Hospital), Andreas Glenthøj(University of Copenhagen), Carl Lander(Thrive), Yan Yan(Wuhan University), Junlong Li(First Teaching Hospital of Tianjin University of Traditional Chinese Medicine), Hitoshi Kanno(Tokyo Women's Medical University), Dagmar Pospı́šilová(Palacký University Olomouc), Eduard J. van Beers(Utrecht University), D. Mark Layton(Imperial College Healthcare NHS Trust), Audra Boscoe(Cambridge University Hospitals NHS Foundation Trust)
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