A luciferase reporter mouse model to optimize in vivo gene editing validated by lipid nanoparticle delivery of adenine base editors
Si-Yue Yu(University of British Columbia), Colin J.D. Ross(BC Children's Hospital), Genc Basha(University of British Columbia), Tiffany Carlaw(University of British Columbia), Linhua Zhang(Chinese Academy of Medical Sciences & Peking Union Medical College), Tyler Thomson(University of Toronto), Alexandra Birkenshaw(University of British Columbia), Jayesh A. Kulkarni(FPInnovations), Cassie Huang(University of Pennsylvania), Daniel Z. Kurek(FPInnovations)
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