Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy
Sharla M. Birch(Texas A&M University), Joe N. Kornegay(Texas A&M University), Cynthia Balog-Alvarez(Texas A&M University), Brittany A. Fickau(Medical College of Wisconsin), Thomas J. Conlon(University of Florida), Michael W. Lawlor(Medical College of Wisconsin), Diane Golebiowski(University of Massachusetts Chan Medical School), Joel Schneider(Solidus Biosciences (United States)), Eleanor C. Hawkins(North Carolina State University), Margaret Beatka(Medical College of Wisconsin), Kristy J. Brown(Children's National), Jeffrey S. Chamberlain(University of Washington), Hui Meng(Medical College of Wisconsin), Martin Styner(University of North Carolina at Chapel Hill), Kirsten E. Coleman(University of Florida), Stephen D. Hauschka(University of Washington), Amanda K. Bettis(Texas A&M University), Julie M. Crudele(University of Washington), Peter P. Nghiem(Texas A&M University), Dongsheng Duan(University of Missouri), Barry J. Byrne(University of Florida), Carl Morris(Sylvana Research), Michael J. Struharik(Solidus Biosciences (United States)), Lee‐Jae Guo(Texas A&M University), Mihye Ahn(University of Nevada, Reno), Xiufang Pan(University of Missouri), Juan Carlos Prieto(University of Chile), J. Patrick Gonzalez(Solidus Biosciences (United States)), Nathalie Clément(University of Florida), Courtney Shanks(Solidus Biosciences (United States)), Manuela Corti(University of Florida)
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