In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
Christopher E. Nelson(Duke University), Charles A. Gersbach(Duke University), David G. Ousterout(Profectus Biosciences (United States)), Sarina Madhavan(Duke University), Dongsheng Duan(University of Missouri), Ruth M. Castellanos Rivera(University of North Carolina at Chapel Hill), Chady H. Hakim(National Center for Advancing Translational Sciences), Eirik A. Moreb(Duke University), Xiufang Pan(University of Missouri), Feng Zhang(Broad Institute), Winston X. Yan, Aravind Asokan(Duke University), F. Ann Ran(Harvard University), Pratiksha I. Thakore(Broad Institute)
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