CRISPR/Cas9 Genome-Edited Autologous Hematopoietic Stem Cell Transplantation Therapies for Sickle Cell Disease

Yi Liu(The University of Texas Southwestern Medical Center), Susan C. Stevenson(Clinical Trial Investigators), Azeddine Elhajouji(Novartis (Switzerland)), Qí Zhāng(Beijing Institute of Genomics), Daher Ibrahim Aibo(Novartis (United States)), Craig Mickanin, Yi Yang(Chinese Academy of Sciences), K. Mueller(Novartis (Switzerland)), Karin Abitorabi(Novartis (Switzerland)), Timothy K. MacLachlan(Novartis (United States)), Daniel J. O’Connell(Harvard University), Vionnie W. Yu, Bo Han(Zhejiang University of Technology), Alberto Del Río-Espínola(Novartis (United States)), Nishit Patel(Intellia Therapeutics (United States)), Carsten Russ(Broad Institute), Madhura Panditrao
Blood
November 15, 2022
Cited by 0


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