Efficient Downregulation of <i>Alk4</i> in Skeletal Muscle After Systemic Treatment with Conjugated siRNAs in a Mouse Model for Duchenne Muscular Dystrophy
Sarah Engelbeen(German Institute of Human Nutrition), Maaike van Putten(Leiden University Medical Center), Laura Sepp‐Lorenzino(Intellia Therapeutics (United States)), Rubina Parmar(Alnylam Pharmaceuticals (United States)), Muthiah Manoharan(Alnylam Pharmaceuticals (United States)), Svetlana Pasteuning-Vuhman(Leiden University Medical Center), Klaus Charissé(Alnylam Pharmaceuticals (United States)), Annemieke Aartsma‐Rus(Leiden University Medical Center)
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