In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
Xiufang Pan(University of Missouri), Dongsheng Duan(University of Missouri), Pratiksha I. Thakore(Broad Institute), David G. Ousterout(Profectus Biosciences (United States)), Sarina Madhavan(Duke University), Charles A. Gersbach(Duke University), Ruth M. Castellanos Rivera(University of North Carolina at Chapel Hill), Chady H. Hakim(National Center for Advancing Translational Sciences), Eirik A. Moreb(Duke University), Feng Zhang(Affiliated Hospital of North Sichuan Medical College), Winston X. Yan, Aravind Asokan(Duke University), F. Ann Ran(Harvard University), Christopher E. Nelson(Duke University)
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