BASELINE DISEASE CHARACTERISTICS OF 47 PEDIATRIC CLASSIC GALACTOSEMIA PATIENTS IN THE ACTION-GALACTOSEMIA KIDS AT-007 INTERVENTIONAL STUDY DEMONSTRATE THE MULTI-SYSTEM BURDEN OF DISEASE
Riccardo Perfetti(Inserm), Shoshana Shendelman(Io Therapeutics (United States)), Francesca Lawson(Sanofi (United States)), Laura Saltonstall, Ayesha Ahmad(University of Michigan), Janet A. Thomas(University of Colorado Denver), H. Phan(Rare Disease Therapeutics (United States)), Evan Bailey
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