Clinical and genetic characteristics of two patients with tyrosinemia type 1 in Slovenia – A novel fumarylacetoacetate hydrolase (FAH) intronic disease-causing variant

Jaka Šikonja(University of Ljubljana), Urh Grošelj(Flinders University), Barbara Faganel Kotnik(Ljubljana University Medical Centre), Barbka Repič Lampret(Ljubljana University Medical Centre), Simona Klemenčič(Ljubljana University Medical Centre), Tadej Battelino(University of Ljubljana), Markéta Tesařová(Charles University), Jernej Brecelj(University of Ljubljana), Maruša Debeljak(University of Ljubljana), Neža Lipovec(Ljubljana University Medical Centre), Ana Drole Torkar(University of Ljubljana), Sara Bertok(Ljubljana University Medical Centre), Mojca Žerjav Tanšek(University of Ljubljana), Valentina Stefanova Kralj(Ljubljana University Medical Centre), Jernej Kovač(University of Ljubljana), Žiga Iztok Remec(Ljubljana University Medical Centre)
Molecular Genetics and Metabolism Reports
December 16, 2021
Cited by 5


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