Variables affecting outcomes after allogeneic hematopoietic stem cell transplant for cerebral adrenoleukodystrophy

Robert Chiesa(Great Ormond Street Hospital), Paul J. Orchard(University of Minnesota), Vinod K. Prasad(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Mattia Algeri(Bambino Gesù Children's Hospital), Nancy Bunin(Children's Hospital of Philadelphia), Alison Timm(Bluebird Bio (United States)), Jörn‐Sven Kühl(Charité - Universitätsmedizin Berlin), Caroline A. Lindemans(University Medical Center Utrecht), Caroline Sevin(Bicêtre Hospital), Simon Jones(Manchester University NHS Foundation Trust), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Esther Shamir(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Neena Kapoor(University of Southern California), Andrew C. Dietz(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Elizabeth McNeil(Bluebird Bio (United States)), Christine Duncan(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Jaap Jan Boelens(Wilhelmina Children's Hospital), Hernán Amartino(Manchester Royal Eye Hospital), Daniel J. Loes(Inserm)
Blood Advances
November 15, 2021
Cited by 40


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