Loss of TBK1 activity leads to TDP-43 proteinopathy through lysosomal dysfunction in human motor neurons

Jin Hao(Zhejiang University Medical College Affiliated Stomatological Hospital), Kevin Eggan(Broad Institute), Zhixun Dou(Université Paris-Saclay), Francesco Limone(New York University), Gengle Niu(Harvard University), Irune Guerra San Juan(Harvard University), Marcel F. Leyton-Jaimes(Broad Institute), Brian Joseph(Columbia University Irving Medical Center), Daniel A. Mordes(University of California, San Francisco), Atsushi Fukuda(Broad Institute), Bogdan Budnik(Unknown), Menglu Qian(Broad Institute), Michael F. Wells(University of California, Los Angeles)
bioRxiv (Cold Spring Harbor Laboratory)
October 12, 2021
Cited by 19


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