Lipid nanoparticle-mediated codelivery of Cas9 mRNA and single-guide RNA achieves liver-specific in vivo genome editing of <i>Angptl3</i>

Min Qiu(Kunming Institute of Botany), Qiaobing Xu(Tufts University), Zachary Glass(Tufts University), Feng Zhang(Microbiology Institute of Shaanxi), Zhongfeng Ye(Tufts University), Xuehui Rui(Tufts University), Xuewei Zhao(Tufts University), Xin Jin(Scripps Research Institute), Yamin Li(Tufts University), Jinjin Chen(Sichuan University), Mary E. Haas(Broad Institute)
Proceedings of the National Academy of Sciences
March 1, 2021
Cited by 390


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