Treatment of autosomal dominant hearing loss by in vivo delivery of genome editing agents

Xue Gao(Xijing Hospital), David R. Liu(Broad Institute), Yong Tao(Shanghai Ninth People's Hospital), Jeffrey R. Holt(Boston Children's Hospital), Verónica Lamas(Massachusetts Eye and Ear Infirmary), Bifeng Pan(Boston Children's Hospital), M. Charles Liberman(Massachusetts Eye and Ear Infirmary), Weijia Kong(Wuhan Union Hospital), Johnny H. Hu(Howard Hughes Medical Institute), Wei-Hsi Yeh(Broad Institute), Yilai Shu(Fudan University), Shiming Yang(Ministry of Education of the People's Republic of China), Daniel B. Polley(Massachusetts Eye and Ear Infirmary), Yamin Li(Tufts University), Yujuan Hu(Union Hospital), Zheng‐Yi Chen(Massachusetts Eye and Ear Infirmary), Mingqian Huang(Nanjing Medical University), David B. Thompson(Howard Hughes Medical Institute), Qiaobing Xu(Tufts University)
Nature
December 18, 2017
Cited by 547


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