AVR-RD-01, an investigational lentiviral gene therapy for Fabry disease: Overview of clinical data from phase 1 and phase 2 studies

Greg Keenan(AVEO Oncology (United States)), Fatemeh Tavakkoli(AVEO Oncology (United States)), Mirjam N. Trame(AVEO Oncology (United States)), Kathy Nicholls(Melbourne Health), B. Carnley(Royal Perth Hospital), Chris Mason(Oak Ridge National Laboratory)
Molecular Genetics and Metabolism
February 1, 2021
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