Mini-COMET study: Effects of repeat avalglucosidase alfa dosing on ptosis in participants with infantile-onset Pompe disease (IOPD) who were previously treated with alglucosidase alfa
James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust), Xianzhang Meng(Jilin Agricultural University), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Si Houn Hahn(University of Washington), Anaïs Brassier(Hôpital Necker-Enfants Malades), Judith Johnson(Sanofi (United States)), David Kronn(New York Medical College), Samia Pichard, Yin‐Hsiu Chien(National Taiwan University Hospital), François Labarthe(Université de Tours), S. Grace Prakalapakorn(Duke University)
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