In vivo cytidine base editing of hepatocytes without detectable off-target mutations in RNA and DNA

Lukas Villiger(University of Zurich), Tanja Rothgangl(University of Zurich), Dominik Witzigmann(University of Basel), Rurika Oka(Oncode Institute), Paulo J.C. Lin(Acuitas Therapeutics (Canada)), Weihong Qi(University of Zurich), Sharan Janjuha(University of Zurich), Christian Berk(ETH Zurich), Femke Ringnalda(ETH Zurich), Mitchell Beattie(Acuitas Therapeutics (Canada)), Markus Stoffel(ETH Zurich), Beat Thöny(Swiss Integrative Center for Human Health), Jonathan Hall(ETH Zurich), Hubert Rehrauer(University of Zurich), Ruben van Boxtel(Oncode Institute), Ying K. Tam(Acuitas Therapeutics (Canada)), Gerald Schwank(University of Zurich)
Nature Biomedical Engineering
January 25, 2021
Cited by 101Open Access
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