NTLA5001, a T Cell Product Candidate with CRISPR-Based Targeted Insertion of a High-Avidity, Natural, WT1-Specific TCR, Shows Efficacy in <i>In Vivo</i> Models of AML and ALL
Eliana Ruggiero(Vita-Salute San Raffaele University), Birgit C. Schultes(Intellia Therapeutics (United States)), Fabio Ciceri(Vita-Salute San Raffaele University), Simo M Arredouani(Intellia Therapeutics (United States)), Laura Sepp‐Lorenzino(Intellia Therapeutics (United States)), Amy M. Becker(Intellia Therapeutics (United States)), Aaron Prodeus(Intellia Therapeutics (United States)), Ivy Dutta(Intellia Therapeutics (United States)), Qingzhan Zhang(University of Illinois Urbana-Champaign), Chiara Bonini(Vita-Salute San Raffaele University), Mark D. McKee(University of Auckland), Maxwell Gabriel Foisey(Intellia Therapeutics (United States)), Dai Liu(Intellia Therapeutics (United States)), Ishina Balwani(Intellia Therapeutics (United States))
Cited by 1
Related Papers
CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
|New England Journal of Medicine|2021|1.7k
Retinoic Acid and Arsenic Trioxide for Acute Promyelocytic Leukemia
|New England Journal of Medicine|2013|1.6k
Gilteritinib or Chemotherapy for Relapsed or Refractory <i>FLT3</i> -Mutated AML
|New England Journal of Medicine|2019|1.3k
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
|New England Journal of Medicine|2009|1k