Cas9 gene therapy for Angelman syndrome traps Ube3a-ATS long non-coding RNA

Justin M. Wolter; Hanqian Mao; Giulia Fragola; Jeremy M. Simon; James L. Krantz; Hannah Bazick; Baris Oztemiz; Jason L. Stein; Mark J. Zylka

doi:10.1038/s41586-020-2835-2

Cas9 gene therapy for Angelman syndrome traps Ube3a-ATS long non-coding RNA

Justin M. Wolter(University of North Carolina at Chapel Hill), Hanqian Mao(University of North Carolina at Chapel Hill), Giulia Fragola(University of North Carolina at Chapel Hill), Jeremy M. Simon(University of North Carolina at Chapel Hill), James L. Krantz(University of North Carolina at Chapel Hill), Hannah Bazick(University of North Carolina at Chapel Hill), Baris Oztemiz(University of North Carolina at Chapel Hill), Jason L. Stein(University of North Carolina at Chapel Hill), Mark J. Zylka(University of North Carolina at Chapel Hill)

Nature

October 21, 2020

10.1038/s41586-020-2835-2

Cited by 166Open Access

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