Lentiviral gene therapy for X-linked chronic granulomatous disease

Donald B. Kohn(University of California, Los Angeles), Claire Booth(Great Ormond Street Hospital for Children NHS Foundation Trust), Elizabeth M. Kang(National Institutes of Health), Sung‐Yun Pai(Boston Children's Hospital), Kit L. Shaw(University of California, Los Angeles), Giorgia Santilli(Great Ormond Street Hospital for Children NHS Foundation Trust), Myriam Armant(Boston Children's Hospital), Karen Buckland(Great Ormond Street Hospital for Children NHS Foundation Trust), Uimook Choi(National Institutes of Health), Suk See De Ravin(National Institutes of Health), Morna J. Dorsey(University of California, San Francisco), Caroline Y. Kuo(University of California, Los Angeles), Diego León‐Rico(Great Ormond Street Hospital for Children NHS Foundation Trust), Christine Rivat(Great Ormond Street Hospital for Children NHS Foundation Trust), Natalia Izotova(Great Ormond Street Hospital for Children NHS Foundation Trust), Kimberly Gilmour(Great Ormond Street Hospital for Children NHS Foundation Trust), Katie Snell(Great Ormond Street Hospital for Children NHS Foundation Trust), Jinhua Xu-Bayford Dip(Great Ormond Street Hospital for Children NHS Foundation Trust), Jinan Darwish(Great Ormond Street Hospital for Children NHS Foundation Trust), Emma Morris(University College London Hospitals NHS Foundation Trust), Dayna Terrazas(University of California, Los Angeles), Leo D. Wang(Boston Children's Hospital), Christopher Bauser(Eurofins (Germany)), Tobias Paprotka(Eurofins (Germany)), Douglas B. Kuhns(Leidos (United States)), John Gregg(University of Pennsylvania), Hayley E. Raymond(University of Pennsylvania), J.K. Everett(University of Pennsylvania), Géraldine Honnet(Genethon (France)), Luca Biasco(Great Ormond Street Hospital for Children NHS Foundation Trust), Peter E. Newburger(University of Massachusetts Chan Medical School), Frederic D. Bushman(University of Pennsylvania), Manuel Grez(Georg Speyer Haus), H. Bobby Gaspar(Great Ormond Street Hospital for Children NHS Foundation Trust), David A. Williams(Boston Children's Hospital), Harry L. Malech(National Institutes of Health), Anne Galy(Inserm), Adrian J. Thrasher(Great Ormond Street Hospital for Children NHS Foundation Trust)
Nature Medicine
January 27, 2020
Cited by 251Open Access
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