Transplantation Outcomes for Children with Severe Combined Immune Deficiency (SCID) Have Improved over Time: A 36-Year Summary Report By the Primary Immune Deficiency Treatment Consortium (PIDTC)
Monica S. Thakar(Fred Hutch Cancer Center), Morton J. Cowan(Blood Systems Research Institute), Evan Shereck(Oregon Health & Science University), Kathleen E. Sullivan(University of Pennsylvania), Michael A. Pulsipher(Primary Children's Hospital), Holly Miller(Phoenix Children's Hospital), Geoff D.E. Cuvelier(CancerCare Manitoba), Troy C. Quigg(CHRISTUS Transplant Institute), Harry L. Malech(University of Maryland, Baltimore), Lisa Forbes Satter(Baylor College of Medicine), Sung‐Yun Pai(Dana-Farber Cancer Institute), Alan P. Knutsen(St. Louis Children's Hospital), Tara Bani-Hashemi, Frederick D. Goldman(University of Alabama at Birmingham), David C. Shyr(University of Utah), Brent R. Logan(Cape Town HVTN Immunology Laboratory / Hutchinson Centre Research Institute of South Africa), Caridad Martinez(Baylor College of Medicine), Alfred P. Gillio(University Medical Center), Emi Caywood(Alfred I. duPont Hospital for Children), Shanmuganathan Chandrakasan(Emory University), Christopher C. Dvorak(University of California, San Francisco), Blachy J. Dávila Saldaña(Children's National), Jennifer Heimall(Children's Hospital of Philadelphia), Hesham Eissa(St. Jude Children's Research Hospital), Theodore B. Moore(University of California, Los Angeles), Lolie C. Yu(Louisiana State University), Élie Haddad(Centre Hospitalier Universitaire Sainte-Justine), Mark Vander Lugt(Pediatrics and Genetics), Ami J. Shah(University of California, Los Angeles), Kenneth B. DeSantes(University of Wisconsin–Madison), Jeffrey J. Bednarski(Washington University in St. Louis), Troy R. Torgerson(Allen Institute for Immunology), Sonali Chaudhury(Northwestern University), Angela R. Smith(University of Minnesota Children's Hospital), Sharat Chandra(Cincinnati Children's Hospital Medical Center), Gauri Sunkersett(Johns Hopkins University), Soma Jyonouchi(Children's Hospital of Philadelphia), Lauri M. Burroughs(Fred Hutch Cancer Center), Julie‐An Talano(Dana-Farber Cancer Institute), Victor Aquino(The University of Texas Southwestern Medical Center), Rebecca H. Buckley(Duke Medical Center), Neena Kapoor(University of Southern California), Aleksandra Petrović(Seattle Children's Hospital), Shalini Shenoy(Washington University in St. Louis), Linda M. Griffith(National Institute of Allergy and Infectious Diseases), Richard J. O’Reilly(Memorial Sloan Kettering Cancer Center), Catherine K. Chang, Rolla Abu‐Arja(Nationwide Children's Hospital), Elizabeth Dunn(Midland Regional Hospital Mullingar), Jacob Rozmus(University of British Columbia)
Cited by 3
Related Papers
Tisagenlecleucel in Children and Young Adults with B-Cell Lymphoblastic Leukemia
|New England Journal of Medicine|2018|5.7k
Chronic Granulomatous Disease: Report on a National Registry of 368 Patients
|Medicine|2000|1.7k
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
|New England Journal of Medicine|2009|1k
Early-Onset Stroke and Vasculopathy Associated with Mutations in ADA2
|New England Journal of Medicine|2014|889