Cytosine and adenine base editing of the brain, liver, retina, heart and skeletal muscle of mice via adeno-associated viruses
Jonathan M. Levy(Broad Institute), Wei-Hsi Yeh(Broad Institute), Nachiket Pendse(Massachusetts Eye and Ear Infirmary), Jessie R. Davis(Broad Institute), Erin Hennessey(Massachusetts Eye and Ear Infirmary), Rossano Butcher(Massachusetts Eye and Ear Infirmary), Luke W. Koblan(Broad Institute), Jason Comander(Massachusetts Eye and Ear Infirmary), Qin Liu(Massachusetts Eye and Ear Infirmary), David R. Liu(Broad Institute)
Cited by 496Open Access
Abstract
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