Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models
Yafeng Song(Qinghai Normal University), Hansell H. Stedman(Philadelphia VA Medical Center), Leonard T. Su(University of Pennsylvania), Leon Morales(University of Pennsylvania), Ranjith K. Krishnankutty(University of Pennsylvania), Alock Malik(University of Pennsylvania), Robert A. French(University of Pennsylvania), Xiangping Lu(University of Pennsylvania), Margaret E. Choi(University of Pennsylvania), Joe N. Kornegay(Texas A&M University), Frederick J. Balzer(University of Pennsylvania), Peter P. Nghiem(Texas A&M University), Jake VanBelzen(University of Pennsylvania), Christopher Greer(University of Pennsylvania), Benjamin W. Kozyak(Children's Hospital of Philadelphia), Shira T. Rosenblum(University of Pennsylvania), Andrew Frederick Mead(University of Pennsylvania), Mihail T. Petrov(University of Pennsylvania), Kathleen J. Propert(Translational Therapeutics (United States)), Shangzhen Zhou(Penn Presbyterian Medical Center), Tejvir S. Khurana(California University of Pennsylvania), Marilyn A. Mitchell(University of Pennsylvania), Emanuele Loro(University of Pennsylvania)
Cited by 94
Related Papers
Efficacy and safety of a microsomal triglyceride transfer protein inhibitor in patients with homozygous familial hypercholesterolaemia: a single-arm, open-label, phase 3 study
|The Lancet|2012|739
Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys
|Science Translational Medicine|2013|346
Prognostic factors in neuroblastoma
|Cancer|1987|322
Canine models of Duchenne muscular dystrophy and their use in therapeutic strategies
|Mammalian Genome|2012|178