Efficacy and safety of a microsomal triglyceride transfer protein inhibitor in patients with homozygous familial hypercholesterolaemia: a single-arm, open-label, phase 3 study

Marina Cuchel(University of Pennsylvania), Daniel J. Rader(University of Pennsylvania), Cesare R. Sirtori(University of Milan), A. David Marais(University of Cape Town), Robert A. Hegele(Western University), Giovanni Battista Vigna(University of Ferrara), Emma A. Meagher(Translational Therapeutics (United States)), Maurizio Averna(Instituto di Biofisica), LeAnne T. Bloedon(Esperion Therapeutics (United States)), Dirk Blom(University of Cape Town), Daniel Gaudet(Brigham and Women's Hospital), Hendrik du Toit Theron(Netcare Unitas Hospital), William J. Sasiela(Inserm), Kathleen J. Propert(Translational Therapeutics (United States)), Prediman K. Shah(Cedars-Sinai Medical Center), Anna ME Du Plessis(University of Pretoria), Claudia Stefanutti(Sapienza University of Rome)
The Lancet
November 2, 2012
Cited by 739


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