Mortality and respiratory support in X-linked myotubular myopathy: a RECENSUS retrospective analysis
Robert J. Graham(Boston Children's Hospital), Alan H. Beggs(Boston Children's Hospital), Tmirah Haselkorn, Imelda Hughes(Manchester University NHS Foundation Trust), Michele Yang(Children's Hospital Colorado), Rachel Alvarez(Cure CMD), Mojtaba Noursalehi(Vital Therapies (United States)), Barry J. Byrne(University of Florida), Laurie LaRusso(Chestnut Hill College), Francesco Muntoni(Great Ormond Street Hospital), Casie A. Genetti(Boston Children's Hospital), Emma S. James(Vital Therapies (United States)), Salvador Rico(Vital Therapies (United States)), Suyash Prasad(Vital Therapies (United States)), Nancy L. Kuntz(Lurie Children's Hospital)
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