Human genome-edited hematopoietic stem cells phenotypically correct Mucopolysaccharidosis type I
Natalia Gomez‐Ospina(Stanford Medicine), Matthew H. Porteus(Stanford University)
Cited by 127
Related Papers
Spermatogonial Stem Cell Self-Renewal Requires OCT4, a Factor Downregulated During Retinoic Acid-Induced Differentiation
|Stem Cells|2008|219
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cells
|Nature Communications|2024|27
Transient Inhibition of 53BP1 Increases the Frequency of Targeted Integration in Human Hematopoietic Stem and Progenitor Cells
|Research Square|2023|2
CNS Repopulation by Hematopoietic-Derived Microglia-Like Cells Corrects Progranulin deficiency
|Research Square|2023|1
Combining Cell-Intrinsic and -Extrinsic Resistance to HIV-1 By Engineering Hematopoietic Stem Cells for CCR5 Knockout and B Cell Secretion of Therapeutic Antibodies
|bioRxiv (Cold Spring Harbor Laboratory)|2024|1