Therapeutically relevant engraftment of a CRISPR-Cas9–edited HSC-enriched population with HbF reactivation in nonhuman primates
Olivier Humbert(Fred Hutch Cancer Center), Hans‐Peter Kiem(Fred Hutch Cancer Center), David J. Rawlings(Center for Infectious Disease Research), Christopher T. Lux, Christopher W. Peterson(University of Washington), Jennifer E. Adair(University of Massachusetts Chan Medical School), Clare Samuelson(Sheffield Teaching Hospitals NHS Foundation Trust), Ciaran M. Lee(University College Cork), Stefan Radtke(Fred Hutch Cancer Center), Gang Bao(Tianjin Stomatological Hospital), Lauren E. Schefter(Fred Hutch Cancer Center), Olivier Nègre(Inserm), Andrew M. Scharenberg(CTI BioPharma (Italy)), Sowmya Reddy(Fred Hutch Cancer Center), Sowmya Pattabhi, Ray R. Carrillo(Fred Hutch Cancer Center), Anai M. Perez(Fred Hutch Cancer Center)
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