Long-term safety and efficacy of glycerol phenylbutyrate for the management of urea cycle disorder patients
George A. Díaz(Icahn School of Medicine at Mount Sinai), Susan A. Berry(University of Minnesota), Cary O. Harding(Oregon Health & Science University), Andreas Schulze(University of Toronto), Colleen Canavan(Horizon Therapeutics (United States)), J. Lawrence Merritt(University of Washington), Jerry Vockley(Pittsburgh Public Schools), Derek A. Wong(University of California, Los Angeles), Shawn E. McCandless(University of Colorado Denver), William Berquist(Palo Alto University), Wendy E. Smith(Maine Medical Center), Thomas Vescio(Horizon Therapeutics (United States)), Dennis Bartholomew(Nationwide Children's Hospital), Robert J. Holt(Horizon Therapeutics (United States)), Uta Lichter‐Konecki(Children's National), Nicola Longo(Center for Human Genetics), Annette Feigenbaum(Hospital for Sick Children), Roberto Zori(University of Florida), Renata C. Gallagher(Children's Hospital Colorado), William J. Rhead(Children's Hospital of Wisconsin)
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